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The Pathway from Gene Therapy to Genome Editing: A Nightmare or Dream
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Mandana Hasanzad1    , Bagher Larijani 2 |
1- Medical Genomics Research Center, Tehran Medical Sciences, Islamic Azad University, Tehran, Iran; Personalized Medicine Research Center, Endocrinology and Metabolism Clinical Sciences Institute, Tehran University of Medical Sciences, Tehran, Iran.
2- Personalized Medicine Research Center, Endocrinology and Metabolism Clinical Sciences Institute, Tehran University of Medical Sciences, Tehran, Iran. , Larijanib1340@gmail.com |
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Abstract: (4382 Views) |
The gene therapy approach has largely been improved by the development of new methods in gene transfer and genome editing. The use of CART cells was first approved in 2018 by FDA for ex vivo treatment of B cell acute lymphoblastic leukemia and in vivo treatment of retinal dystrophy. This revolutionary trend is expected to continue as the clinical vision develops and the technical capacity improves. |
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| Keywords: Gene Therapy, Genome Editing |
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Full-Text [PDF 337 kb]
(1468 Downloads)
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Type of Study: Letters to the editor |
Subject:
Other
Received: 2019/03/13 | Accepted: 2019/11/9 | Published: 2020/01/1
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